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CheckOrphan NewsFlash, March 2,…
3/02/2010
CheckOrphan NewsFlash for Tuesday, March 2, 2010: breaking news about rare diseases, orphan diseases, orphan drugs, and…
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CheckOrphan NewsFlash January 15,…
1/15/2010
CheckOrphan NewsFlash for Friday, January 15, 2010: breaking news about rare diseases, orphan diseases, orphan drugs,…
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CheckOrphan NewsFlash January 11,…
1/11/2010
CheckOrphan NewsFlash for Monday, January 11, 2010: breaking news about rare diseases, orphan diseases, orphan drugs,…
NewsFlash
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Brain, Blood, and Iron: Advances…
13–14 March, 2010
The overall objectives of this workshop are to: (1) define NA and NBIA…
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Diamond Blackfan Anemia…
13–15 March, 2010
This conference is expected to generate immediate and long-term…
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Interdisciplinary Training…
15–16 March, 2010
The goal of this meeting is to mentor the career development of a “…
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ICORD 2010: Sixth International…
18–20 March, 2010
The VI International Conference on Rare Diseases and Orphan Drugs (ICORD…
Events
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'Rare' Cancers in the Spotlight at Major European Conference
Thursday, February 25, 2010
More should be done across Europe to ensure that people with rare forms of cancer are not denied access to the best possible treatment, say the organizers of a major European cancer conference to be held in Milan on 9 and 10 March 2010"People with rare diseases have the same right to receive prope
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Ark Therapeutics Files Cerepro(R) Re-Examination Documentation With the European Medicines Agency
Wednesday, February 24, 2010
London, UK -- Ark Therapeutics Group plc (AKT: LSE) ("Ark" or "the Company"), announces that it has filed documentation with the European Medicines Agency ("EMA") in relation to its request for re-examination of the marketing approval application ("MAA") for Cerepro®, Ark's novel gene based Th
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Aradigm Doses First Patient in Its Second Phase 2b Clinical Trial of Inhaled Liposomal Ciprofloxacin in Bronchiectasis Patients
Wednesday, February 24, 2010
HAYWARD, Calif. -- Aradigm Corporation (OTCBB:ARDM) (the "Company") today announced that it dosed the first patient in the U.S. as part of its ORBIT-1 (Once-daily Respiratory Bronchiectasis Inhalation Treatment) trial, an international, randomized, double-blind, placebo-controlled Phase 2b study T
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Mayo Oral Cancer Study Shows Full Tumor Genome
Wednesday, February 24, 2010
ROCHESTER, Minn. -- Mayo Clinic researchers along with collaborators from Life Technologies are reporting on the application of a new approach for sequencing RNA to study cancer tumors. Their findings from a proof-of-principle study on oral carcinomas appear in the current issue of PLoS One, the V
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Reco® Jeans Supports Children With Rare Diseases
Wednesday, February 24, 2010
NEW YORK -- reco® jeans (www.recojeans.com), the leading manufacturer of true recycled denim jeans, today announced the company will create a special denim ribbon in support of the Global Genes Project (www.globalgenesproject.org), an initiative designed to raise awareness about the prevalence
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U.S. Food and Drug Administration Approves Cayston(R) (Aztreonam for Inhalation Solution) for the Improvement of Respiratory Symptoms in Cystic Fibrosis Patients With Pseudomonas Aeruginosa
Wednesday, February 24, 2010
FOSTER CITY, Calif. -- Gilead Sciences, Inc. (Nasdaq:GILD) today announced that the U.S. Food and Drug Administration (FDA) has granted marketing approval for Cayston(R)(aztreonam for inhalation solution) as a treatment to improve respiratory symptoms in cystic fibrosis (CF) patients with Cayston'
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FDA Approves Once-Daily MIRAPEX ER for the Treatment of Early Parkinson's Disease
Tuesday, February 23, 2010
RIDGEFIELD, Conn. -- Boehringer Ingelheim Pharmaceuticals, Inc., today announced that the U.S. Food and Drug Administration (FDA) has approved Mirapex ER® (pramipexole dihydrochloride) extended-release tablets, a new once-daily treatment option for the signs and symptoms of early idiopathic MI
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Despite Minimal Uptake in the Crohn's Disease Drug Market, Stelara's Premium Price Will Result in Sales of Nearly $337 Million in 2018
Tuesday, February 23, 2010
WALTHAM, Mass. -- Decision Resources, one of the world's leading research and advisory firms for pharmaceutical and healthcare issues, finds that, in the Crohn's disease drug market, the premium price of Centocor Ortho Biotech/Janssen-Cilag's Stelara and Abbott's briakinumab will drive robust sales
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Merrimack Pharmaceuticals Initiates Enrollment in a Phase 1/2 Combination Study of MM-121 and Tarceva(R) in Patients With Non-Small Cell Lung Cancer
Tuesday, February 23, 2010
CAMBRIDGE, Mass. -- Merrimack Pharmaceuticals, Inc. announced today that the first patient has received an initial dose in a Phase 1/2 clinical study combining MM-121 with Tarceva® (erlotinib) in patients with non-small cell lung cancer (NSCLCThis is the first of multiple trials that Merrimack
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NIH Grant Will Create Behavioral Health Registry for Pediatric Inflammatory Bowel Disease
Tuesday, February 23, 2010
PROVIDENCE, RI -- The National Institutes of Health has awarded a two-year development grant to researchers with Hasbro Children's Hospital and the Bradley Hasbro Children's Research Center to better understand the role behavioral health plays in pediatric inflammatory bowel disease (IBD), a The $
