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CheckOrphan NewsFlash, March 2,…
3/02/2010
CheckOrphan NewsFlash for Tuesday, March 2, 2010: breaking news about rare diseases, orphan diseases, orphan drugs, and…
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CheckOrphan NewsFlash January 15,…
1/15/2010
CheckOrphan NewsFlash for Friday, January 15, 2010: breaking news about rare diseases, orphan diseases, orphan drugs,…
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CheckOrphan NewsFlash January 11,…
1/11/2010
CheckOrphan NewsFlash for Monday, January 11, 2010: breaking news about rare diseases, orphan diseases, orphan drugs,…
NewsFlash
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Interdisciplinary Training…
15–16 March, 2010
The goal of this meeting is to mentor the career development of a “…
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ICORD 2010: Sixth International…
18–20 March, 2010
The VI International Conference on Rare Diseases and Orphan Drugs (ICORD…
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Improving Musculoskeletal Outcomes…
7–9 April, 2010
The goals of this workshop are to (1) assess the state of knowledge…
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Third NIH Workshop on Gaucher…
8–9 April, 2010
Workshop goals are to (1) determine the appropriate human, animal, or cell…
Events
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NPS Pharmaceuticals Announces Support for Rare Disease Day Observance
Friday, February 26, 2010
BEDMINSTER, N.J. -- NPS Pharmaceuticals, a specialty pharmaceutical company developing innovative therapeutics for rare gastrointestinal and endocrine disorders, announced today its support for the second annual U.S. Rare Disease Day observance on February 28Rare Disease Day aims to call attention
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Combined Drug Therapy to Treat TB and HIV Significantly Improves Survival
Friday, February 26, 2010
Initiating antiretroviral therapy (ART) during tuberculosis therapy significantly reduced mortality rates by 56 percent in a randomized clinical trial of 642 patients co-infected with HIV and tuberculosisThe study, which provides further impetus for the integration of TB and HIV services, lays to
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Alexion Joins NORD, EURORDIS and Other Patient Advocacy Groups in Supporting the Goals of Rare Disease Day 2010
Friday, February 26, 2010
CHESHIRE, Conn. & SMITHFIELD, R.I. -- Alexion Pharmaceuticals, Inc., (Nasdaq: ALXN) has joined the National Organization for Rare Disorders (NORD) and the European Organization for Rare Diseases (EURORDIS) in supporting the goals of the third annual Rare Disease Day, February 28, 2010Rare Dise
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Rare Disease Advocates Unite to Translate Slogan of Global Genes Project in Time for World Rare Disease Day!
Friday, February 26, 2010
DANA POINT, CA -- The Global Genes Project (www.globalgenesproject.org), today announced that its rare disease campaign slogan, “Hope It’s In Our Genes ,” has been translated into multiple international languages and Braille by rare disease patient advocates and supporters from T
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FDA Approves First New Inhaled Antibiotic for CF in More Than a Decade
Thursday, February 25, 2010
BETHESDA, Md. -- The U.S. Food and Drug Administration approved an important new inhaled antibiotic called Cayston® (aztreonam for inhalation solution) today for the treatment of cystic fibrosisThe drug was made possible by significant support from the Cystic Fibrosis Foundation, including a $
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PharmAthene Awarded Up to Additional $78.4 Million Under Existing Contract for Advanced Development of SparVax(TM) Anthrax Vaccine
Thursday, February 25, 2010
ANNAPOLIS, Md. -- PharmAthene, Inc. (NYSE Amex: PIP) a biodefense company specializing in the development and commercialization of medical countermeasures against chemical and biological threats, announced today that the Department of Health and Human Services (HHS), through the Biomedical Advanced
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North Carolina Couple Finds Hope for a Healthy Baby Through Technology That Screens Embryos for Genetic Disorders
Thursday, February 25, 2010
RALEIGH, N.C. -- After a devastating loss of their five month old son to a genetically linked disease, a North Carolina couple finds hope for a healthy baby through an innovative technology called Preimplantation Genetic Diagnosis (PGDUsing embryo biopsy, PGD allows geneticists to screen for disor
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International Rare Disease Day
Thursday, February 25, 2010
PARIS- "Patients and Researchers: Partners for Life- 28 February Marks the Third Rare Disease DayFor this annual event hundreds of patient groups and their partners organise activities to raise awareness on rare diseases and the 30 million people affected by them in EuropeRare Disease Day was l
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Data Show Valortim(R) Anthrax Anti-Toxin May Augment Immune System's Ability to Destroy Anthrax Bacteria
Thursday, February 25, 2010
ANNAPOLIS, Md. -- PharmAthene, Inc. (NYSE Amex: PIP), a biodefense company developing medical countermeasures against biological and chemical threats, announced today that new data from the Company's Valortim® anthrax anti-toxin program were presented at the 8th Annual ASM Biodefense and The d
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Guidepoint Global Announces Launch of Genetic Disorder Tracker
Thursday, February 25, 2010
NEW YORK -- Guidepoint Global, LLC, a leading primary research firm, today announced the launch of their Genetic Disorder Tracker, a monthly longitudinal data release that captures commercial trends, on a worldwide basis, associated with the treatment of eight rare genetic disorders: Gaucher's Gui
